- CRISPR-Cas9 gene editing successful for a patient with Sickle Cell Disease and another patient with transfusion dependent β-Thalassemia - More than a year later, both patients had clinically improved and no longer needed blood transfusions. (NEJM, 5 Dec 2020) https://www.nejm.org/doi/full/10.1056/nejmoa2031054 461 comments science
Linking pages
- Opinion | CRISPR Can Cure Disease by Editing a Person’s DNA. Now What? - The New York Times https://www.nytimes.com/2022/12/09/opinion/crispr-gene-editing-cures.html 47 comments
- Pioneering Gene Therapy Freed Her of Sickle Cell. Is a Cure at Hand? - The New York Times https://www.nytimes.com/2021/09/14/health/sickle-cell-cure.html?campaign_id=34&emc=edit_sc_20210914&instance_id=40348&nl=science-times®i_id=54686661&segment_id=68867&te=1&user_id=b6f64731b0a6fa745bdbb088a7aed02f 29 comments
- Biologic and Clinical Efficacy of LentiGlobin for Sickle Cell Disease | NEJM https://www.nejm.org/doi/full/10.1056/NEJMoa2117175 2 comments
- New gene editing tool offers promise of treating many genetic diseases https://www.usatoday.com/story/news/health/2021/01/06/new-gene-editing-tool-offers-promise-treating-many-genetic-diseases-progeria/6556277002/ 1 comment
- 2020 Was a Breakout Year for Crispr | WIRED https://www.wired.com/story/2020-was-a-breakout-year-for-crispr/ 0 comments
- CRISPR gene editing may help treat heart disease after a heart attack https://www.medicalnewstoday.com/articles/heart-disease-crispr-gene-editing-may-repair-damaged-tissue-after-heart-attack 0 comments
- Opinion | A New Sickle Cell Treatment Will Change Lives — but How Many? - The New York Times https://www.nytimes.com/2023/10/30/opinion/sickle-cell-gene-therapy-crispr.html 0 comments
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